Therapeutic goals in Fabry disease: Recommendations of a European expert panel, based on current clinical evidence with enzyme replacement therapy

Christoph Wanner, Dominique P. Germain, Max J. Hilz, Marco Spada, Bruno Falissard, Perry M. Elliott

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
JournalMolecular Genetics and Metabolism
DOIs
Publication statusAccepted/In press - Jan 1 2018

ASJC Scopus subject areas

  • Endocrinology, Diabetes and Metabolism
  • Biochemistry
  • Molecular Biology
  • Genetics
  • Endocrinology

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