In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of β-thalassemia

Annarita Miccio, Rossano Cesari, Francesco Lotti, Claudia Rossi, Francesca Sanvito, Maurilio Ponzoni, Samantha J E Routledge, Cheok Man Chow, Michael N. Antoniou, Giuliana Ferrari

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Medicine & Life Sciences