Good Laboratory Practice Preclinical Safety Studies for GSK2696273 (MLV Vector-Based Ex Vivo Gene Therapy for Adenosine Deaminase Deficiency Severe Combined Immunodeficiency) in NSG Mice

N Carriglio, J Klapwijk, RJ Hernandez, M Vezzoli, F Chanut, R Lowe, Elena Draghici, M Nord, P. Albertini, P Cristofori, J Richards, H Staton, J Appleby, A Aiuti, AV Sauer

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