Evaluation of ADA gene expression and transduction efficiency in ADA/SCID patients undergoing gene therapy

F. Carlucci, A. Tabucchi, A. Aiuti, F. Rosi, F. Floccari, R. Pagani, E. Marinello

Research output: Contribution to journalArticlepeer-review

Abstract

A capillary electrophoresis (CE) method was developed for ADA/SCID diagnosis and monitoring of enzyme replacement therapy, as well as for exploring the transfection efficiency for different retroviral vectors in gene therapy.

Original languageEnglish
Pages (from-to)1245-1248
Number of pages4
JournalNucleosides, Nucleotides and Nucleic Acids
Volume23
Issue number8-9
DOIs
Publication statusPublished - 2004

Keywords

  • ADA/SCID
  • Capillary electrophoresis
  • Gene therapy

ASJC Scopus subject areas

  • Biochemistry
  • Genetics

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